Systemic AAV-Mediated β-Sarcoglycan Delivery Targeting Cardiac and Skeletal Muscle Ameliorates Histological and Functional Deficits in LGMD2E Mice
Pozsgai ER1, Griffin DA2, Heller KN2, Mendell JR3, Rodino-Klapac LR4.
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Pozsgai ER1, Griffin DA2, Heller KN2, Mendell JR3, Rodino-Klapac LR4.