Efficient exon skipping of SGCG mutations mediated by phosphorodiamidate morpholino oligomers

JCI Insight . 2018 May 3;3(9):e99357. doi: 10.1172/jci.insight.99357.

Eugene J Wyatt 1, Alexis R Demonbreun 1, Ellis Y Kim 2, Megan J Puckelwartz 1, Andy H Vo 3, Lisa M Dellefave-Castillo 1, Quan Q Gao 4, Mariz Vainzof 5, Rita C M Pavanello 5, Mayana Zatz 5, Elizabeth M McNally 1

Affiliations expand
PMID: 29720576 PMCID: PMC6012523 DOI: 10.1172/jci.insight.99357

Free PMC article
https://pubmed.ncbi.nlm.nih.gov/29720576/