β-Sarcoglycan gene transfer decreases fibrosis and restores force in LGMD2E mice
Gene Therapy , (20 August 2015) | doi:10.1038/gt.2015.80
E R Pozsgai, D A Griffin, K N Heller, J R Mendell and L R Rodino-Klapac
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Gene Therapy , (20 August 2015) | doi:10.1038/gt.2015.80
E R Pozsgai, D A Griffin, K N Heller, J R Mendell and L R Rodino-Klapac